Bluebird Bio (BLUE - Get Report) is presenting some preliminary clinical trial results Wednesday showing its gene therapy is stabilizing a small number of young boys with an extremely rare, and fatal, inherited neurological disease. The disease is cerebral adrenoleukodystrophy, or CALD. Boys are affected primarily because the disease is inherited through a defective X chromosome carried by the mother. CALD causes the progressive destruction of a protective sheath around nerves cells in the brain responsible for...
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